The FDA has lifted its hold and has given Entrada Therapeutics permission to launch a Phase 1b clinical trial to test ...

Reflecting on his sudden hospitalization last year, columnist Patrick Moeschen emphasizes the need to create an emergency medical plan.

People with Duchenne or Becker muscular dystrophy who had more siblings typically report being better prepared to transition ...

Five oculopharyngeal muscular dystrophy (OPMD) patients have now been treated with the gene therapy candidate BB-301 in a ...

Columnist Betty Vertin, overwhelmed by caregiving duties and decisions, sometimes feels like she's walking a tightrope.

FSHD has made an increasing number of everyday items unusable for columnist Robin Stemple because they're too heavy.

Enrollment of healthy volunteers for a Phase 1 trial testing Duchenne muscular dystrophy (DMD) treatment candidate SAT-3247 ...

I’ll be straightforward about caregiving: It’s exhausting. I’m the mother of seven children: Lexi, 23, Max, 19, Chance, 17, Rowen, 16, Charlie, 14, Mary, 10 ...